Moving the Needle on ALS & Neuromuscular Disorders


Dear colleagues and friends,


We’re excited to share with you the full agenda below for our rare disease virtual event, “Moving the Needle on ALS & Neuromuscular Disorders,” which will premiere on June 21st the Global ALS/MND Awareness Day as we continue to shape new thinking in advancing breakthroughs for patients. This complimentary webinar will bring together leading clinicians, patient advocates, researchers, and drug developers who are working together to raise awareness for and overcome barriers to find a cure for ALS and neuromuscular disorders. 


Please click here to reserve your event pass. Click here for event speakers’ bios and program updates. To accommodate our international audience, this event will premiere from 8:00am – 10:30am PDT (11:00am – 1:30pm EDT), and again from 7:00pm – 9:30pm PDT (10:00pm – 12:30am EDT). For the convenience of our attendees, we will provide all registrants with an on-demand recording after the event.


AGENDA (The time below is AM, Pacific Daylight Time | Virtual via Zoom)


8:00 Welcome

Hui Cai, Program Chair, VP & Head of Content, WuXi AppTec

Calaneet Balas, President & CEO, The ALS Association

Lin Kah Ooi, Founding President, Motor Neurone Disease Association Singapore


8:10 The Unmet Needs in Neuromuscular Disorders

Carsten Bönnemann, Senior Investigator, Neuromuscular & Neurogenetic Disorders of Childhood Section, NINDS

Matthew Harms, Associate Professor of Neurology, Institute for Genomic Medicine, Columbia University

Moderator: Sharon Hesterlee, Chief Research Officer, Muscular Dystrophy Association


8:40 Spotlight on ALS

Kuldip Dave, SVP of Research, The ALS Association

Sabrina Paganoni, Co-Director, Neurological Research Institute at Massachusetts General Hospital; Physician Scientist, Healey & AMG Center for ALS

Jeffrey Rothstein, Director of Brain Science Institute, Director, Robert Packard Center for ALS Research, Johns Hopkins University


9:10 In the Pipeline

Neil Cashman, CSO, ProMIS Neurosciences; Professor Emeritus, University of British Columbia

Michael McGrath, UCSF Emeritus Professor of Medicine; CSO & Founder, Neuvivo

Robert Scannevin, CSO, Verge Genomics

Fernando Vieira, CEO & CSO, ALS Therapy Development Institute

Moderator: Murali Gopalakrishnan, Global Head, Neuroscience Search & Evaluation, Corporate Strategy Office, AbbVie


9:50 Challenges and Opportunities in New Modalities

Jim Burns, CEO, Locanabio

Clive Svendsen, Professor & Executive Director, Board of Governors Regenerative Medicine Institute

Moderator: Bibhash Mukhopadhyay, Managing Partner, Sound Bioventures


10:20 The Future of Genetic and Personalized Medicines

Michael Snyder, Professor & Chair, Department of Genetics; Director, Center for Genomics and Personalized Medicine, Stanford University


10:25 Closing Remarks

Richard Soll, Head of Boston Office and Senior Advisor of Strategic Initiatives, WuXi AppTec


Register Now