Moving the Needle on ALS & Neuromuscular Disorders



Dear colleagues and friends,

We are honored to have been able to unite 3,000+ colleagues this year from around the world for our virtual event, “Moving the Needle on ALS & Neuromuscular Disorders,” on June 21st, 2022. Together we were able to enhance awareness and provide a global stage for key stakeholders to connect and collaborate to overcome barriers to finding cures for these devastating rare diseases.

This is our 9th episode of our “Collaborations That Transform” series. At WuXi AppTec, we are dedicated to providing a platform to catalyze transformational change for patients.

Special thanks to our more than 20 distinguished speakers, and to our supportive partners: ALS AssociationMuscular Dystrophy AssociationMotor Neurone Disease Association Singapore, and Beijing Oriental Rain ALS Care Center.

You are welcome to watch this event on-demand here:

Thank you again, and make sure to follow us on Twitter and LinkedIn, and visit our WXPress website to stay up-to-date on upcoming WuXi AppTec news and events.

If you have any questions, please contact us at

AGENDA (The time below is AM, Pacific Daylight Time | Virtual via Zoom)


8:00 Welcome

Hui Cai, Program Chair, VP & Head of Content, WuXi AppTec

Calaneet Balas, President & CEO, The ALS Association

Lin Kah Ooi, Founding President, Motor Neurone Disease Association Singapore


8:10 The Unmet Needs in Neuromuscular Disorders

Carsten Bönnemann, Senior Investigator, Neuromuscular & Neurogenetic Disorders of Childhood Section, NINDS

Matthew Harms, Associate Professor of Neurology, Institute for Genomic Medicine, Columbia University

Moderator: Sharon Hesterlee, Chief Research Officer, Muscular Dystrophy Association


8:40 Spotlight on ALS

Kuldip Dave, SVP of Research, The ALS Association

Sabrina Paganoni, Co-Director, Neurological Research Institute at Massachusetts General Hospital; Physician Scientist, Healey & AMG Center for ALS

Jeffrey Rothstein, Director of Brain Science Institute, Director, Robert Packard Center for ALS Research, Johns Hopkins University


9:10 In the Pipeline

Neil Cashman, CSO, ProMIS Neurosciences; Professor Emeritus, University of British Columbia

Michael McGrath, UCSF Emeritus Professor of Medicine; CSO & Founder, Neuvivo

Robert Scannevin, CSO, Verge Genomics

Fernando Vieira, CEO & CSO, ALS Therapy Development Institute

Moderator: Murali Gopalakrishnan, Global Head, Neuroscience Search & Evaluation, Corporate Strategy Office, AbbVie


9:50 Challenges and Opportunities in New Modalities

Jim Burns, CEO, Locanabio

Clive Svendsen, Professor & Executive Director, Board of Governors Regenerative Medicine Institute

Moderator: Bibhash Mukhopadhyay, Managing Partner, Sound Bioventures


10:20 The Future of Genetic and Personalized Medicines

Michael Snyder, Professor & Chair, Department of Genetics; Director, Center for Genomics and Personalized Medicine, Stanford University


10:25 Closing Remarks

Richard Soll, Head of Boston Office and Senior Advisor of Strategic Initiatives, WuXi AppTec